Gene therapy offers hope for rare retinal condition (The Dana Foundation Website – 7 December 2009)

Dana_logo A one-shot gene therapy may offer sight to children with a rare retinal condition called Leber's congenital amaurosis.  A recent clinical trial of the therapy showed remarkable success.


Three years ago, when
nine-year-old Corey Haas was first diagnosed with Leber’s congenital
amaurosis (LCA), a rare form of retinal degenerative disease, his
parents weren’t given a hopeful prognosis regarding his vision…

(To read the rest of the article, click here).

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